Patients & caregivers
Pediatric oncology is hard. That’s why we’re here.
At Y-mAbs, we don’t think “hard” should be a barrier to progress. Every day, we work to develop new therapies for rare and challenging pediatric cancers so that patients and their families can imagine a better future. Y-mAbs is currently conducting clinical trials in rare diseases, including high-risk neuroblastoma and osteosarcoma.
Follow the link below to learn if your child qualifies for one of our clinical trials.

Expanded access for an investigational medicine
Y-mAbs Therapeutics, Inc. (Y-mAbs) is a company built with a focus on patients with unmet medical needs in oncology. From time to time, we receive inquiries about making Y-mAbs’ investigational medicines available to patients with serious or life-threatening disease or condition for whom enrollment in clinical trials is not an option, and there are no beneficial therapies available.
Y-mAbs has established a process whereby certain patients may gain access to Y-mAbs investigational medicine on an “expanded access” or “compassionate use” basis if certain exceptional criteria are met. This process is available only in certain countries and for limited periods.
Process
For countries in Europe:
DANYELZA® (naxitamab-gqgk) 40mg/10mL Injection may be available to patients contingent on meeting the eligibility criteria in Europe through a Named Patient Program (NPP) subject to receiving local approval.
For more information about, or to be considered for the DANYELZA® Named Patient Program, the patient’s treating physician must first make a request via email to danyelzanpp@wepclinical.com. Further guidance and instructions will then be provided upon receiving this request.
Y-mAbs has established a process whereby certain patients may gain access to Y-mAbs investigational medicine on an “expanded access” or “compassionate use” basis if certain exceptional criteria are met. This process is available only in certain countries and for limited periods.
For countries outside Europe:
For more information about, or to be considered for expanded access / compassionate use, a patient’s treating physician must first make a request via email to clinicaltrials@ymabs.com. Once Y-mAbs has received all of the required information for consideration, an acknowledgement receipt of the request will typically be sent within five (5) business days. If you are a patient or enquiring on behalf of a patient interested in Y-mAbs’ expanded access / compassionate use, please talk to your doctor.
Evaluation criteria
All requests for compassionate use of investigational medicines are carefully considered, and decisions are thoughtfully made based on various factors, with the patient’s safety and well-being at top of mind. However, Y-mAbs cannot guarantee that any specific request will be fulfilled and makes decisions at its sole discretion.
Y-mAbs will evaluate each request based on a variety of criteria and factors, which include but are not limited to the following:
- The patient has a serious or life-threatening disease and there are no beneficial treatment options available;
- The potential benefit of the investigational medicine likely outweighs any potential risks;
- There is an adequate supply of the investigational medicine;
- The patient is either ineligible or cannot participate in on-going clinical trials for the investigational medicine;
- Information to inform the treating physician on the safety and appropriate use of the investigational medicine can be provided;
- Providing access to an investigational medicine does not interfere with the ability to complete patient enrollment and other aspects of the clinical trials necessary to support registration of the investigational medicine; and
- Other factors which Y-mAbs deems appropriate to consider from time to time, in its full discretion.
Y-mAbs reserves the right to revise its expanded access / compassionate use policy in whole or in part at any time, without notice.

Patient and family resources
Along your child’s treatment journey, there are many resources that can be helpful to you, your child, and your family. Here are a few resources that can help explain certain conditions and how to cope with them. For questions regarding treatment and care, please consult with your child’s physician. These resources should not be considered substitutes for professional medical guidance.
A government-run organization that conducts research, training, and outreach efforts to prevent, diagnose, treat, and understand different types of cancer, including neuroblastoma.
A nonprofit organization dedicated to raising awareness, funding research, providing support, and advocating for children and families affected by neuroblastoma.
Advocacy partners
Y-mAbs is proud to partner with the following organizations:
Isabella Santos Foundation, an organization dedicated to supporting research, treatments, and families affected by rare pediatric cancers.
Arms Wide Open Childhood Cancer Foundation, a foundation committed to funding pediatric cancer research, supporting families who are suffering hardship due to their child’s cancer diagnosis both financially and emotionally, educating the general public, raising awareness globally, uniting the childhood cancer community, starting a movement, and giving children with cancer a voice so that they will see change in their lifetime.
CNCF, a nonprofit, national health organization committed to finding a cure to neuroblastoma.
Momcology, a community-based support and advocacy organization providing peer support, education, and community for caregivers of children with cancer.
Evan’s Victory Against Neuroblastoma Foundation (The EVAN Foundation), an organization that supports research, and sponsors the Treats & Treasures Carts Program at select hospitals and clinics across the country.
Solving Kids Cancer, an organization that finds, funds, and advocates for breakthrough childhood cancer treatments.
Candlelighters Childhood Cancer Family Alliance, an alliance that provides emotional, educational, and practical support to families of children with cancer.
Band of Parents Bound by Hope, a nonprofit organization that funds innovative research and clinical trials for neuroblastoma, helping increase the survival rate for this childhood cancer.
Alex’s Lemonade Stand Foundation for Childhood Cancer, a foundation that works to change the lives of children with cancer through funding impactful research, raising awareness, supporting families and empowering everyone to help cure childhood cancer.
Ronald McDonald House Charities, a nonprofit organization whose stated mission is to create, find, and support programs that directly improve the health and well-being of children.
End Kids Cancer, an organization that supports research that harnesses the immune system and offers resources for finding care and overcoming financial and emotional hardships.
Neuroblastoma Children’s Cancer Society. The mission of the Neuroblastoma Children’s Cancer Society is to cure neuroblastoma and its related childhood cancers, as well as to improve the quality of life for patients, survivors, and their families.
Other resources

National Organization for Rare Disorders (NORD)
National Organization for Rare Disorders (NORD) advances practical, meaningful, and enduring change so people with rare diseases can live their fullest and best lives. Every day, we elevate care, advance research, and drive policy in a purposeful and holistic manner to lift up the rare disease community.

The U.S. National Cancer Institute
The U.S. National Cancer Institute’s website provides accurate, up-to-date information about many types of cancer, information about clinical trials, resources for people dealing with cancer, and information for researchers and health professionals. It also leads, conducts, and supports cancer research across the nation to advance scientific knowledge and help all people live longer, healthier lives.

American Cancer Society: Neuroblastoma Tumors
The American Cancer Society has a vision to end cancer as we know it, for everyone. We’re improving the lives of cancer patients and their families through advocacy, research, and patient support to ensure that everyone has an opportunity to prevent, detect, treat, and survive cancer. The American Cancer Society has a vision to end cancer as we know it, for everyone.